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Gene Therapy: Mending a Failing Heart?
By Julie Steenhuysen
(Reuters)—A gene therapy treatment helped people with advanced heart failure pump blood more efficiently without causing serious side effects a year after treatment, researchers said, showing yet more promise for this approach. Mydicar, a treatment made by privately held Celladon of La Jolla, California, delivers an enzyme that becomes deficient in people with advanced heart failure. Read the full article >>.
Testing Autism Drugs in Human Brain Cells
By Jennifer Chu
Autism is a highly complex disorder affecting one in every 110 children born in the United States. The disease's genetic profile and behavioral symptoms fluctuate widely from case to case, and this variability has frustrated scientists' efforts to identify effective treatments. A new study suggests that autism could eventually be a target for personalized treatment, customized to a patient's individual’s neurons. . Read the full article >>
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